-
side effects
- leukemia
-
gene repair
- homologous recombination
- single nucleotide mutation
-
hereditary disease
- homozygous
- heterozygous
- Main Topic 5
-
vector
- retrovirus
- adenovirus
- AAV (adeno associated virus)
- liposome
-
insertion in the genome
- activation of oncogenes
- high transcription
- clinical trial
- emerging field